CRISPR/Cas9 Cell Therapeutics – The Next Generation of Cures
Learn about strategies for using CRIPSR/Cas9 for curing genetic diseases, and the impact on next generation disease model systems and drug screening.
Hosted by GEN, Produced with Support from Lonza
The discovery of CRIPSR/Cas9 as simple and effective tool for targeted modification of cells has opened up new possibilities for gene or cell therapies. We will discuss strategies for using CRIPSR/Cas9 for curing genetic diseases, and the impact on next generation disease model systems and drug screening.
Introduction to CRISPR/Cas9
Application examples with focus on use for sickle cell disease
Opportunities and challenges for the use of CRISPR/Cas9 in gene/cell therapeutic applications
Use of CRISPR for next generation disease model systems
Non-viral transfer of CRISPR/Cas9 cargos and up-scaling of the transfection process
Matt Porteus, MD, PhD, Associate Professor of Pediatrics, Stanford University
Greg Alberts, PhD, Global Subject Matter Expert Transfection and Genome Editing, Lonza Bioscience Solutions
Efficient genome editing using Lonza's NucleofectorTM Technology
On-site Demonstration of 4D-NucleofectorTM Technology
4D-NucleofectorTM X and Y Unit
Are you interested in seeing the NucleofectorTM Technology for medium-throughput applications in your lab and how it performs for your cells? One of our transfection specialists can come to your lab, introduce you to your preferred platform and perform a transfection experiment with your cell type of interest.